NGNENeurogene

About Neurogene
Neurogene (NASDAQ:NGNE) is a biotechnology company developing gene therapy treatments for nervous system disorders. They utilize adeno-associated virus (AAV) vectors to deliver corrective genetic material to target cells, potentially offering a new approach to treating neurological conditions. Neurogene's pipeline might focus on treatments for rare or debilitating diseases with limited therapeutic options. While they are still in the pre-commercial stages, with clinical trials ongoing, Neurogene's gene therapy research holds promise for offering life-changing treatments for patients with neurological conditions.
What is NGNE known for?
Snapshot
Public US
Ownership
2018
Year founded
94
Employees
New York, United States
Head office
1 of 3
US Rank
Unknown
Sector
N/A
Sector rank
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Operations
All Locations
New York City, US
Products and/or services of Neurogene
- Adeno-associated virus (AAV) based gene therapy for neurological diseases, aiming to address genetic disorders by delivering normal genes to patients' cells.
- Development of a gene therapy for Aspartylglucosaminuria (AGU), a rare lysosomal storage disease, focusing on reducing the accumulation of glycoasparagines.
- Gene therapy targeting Charcot-Marie-Tooth Disease, specifically focusing on mutations in the GJB1 gene, aiming to restore normal nerve function.
- Exploration of therapies for Rett Syndrome, a neurodevelopmental disorder, focusing on correcting MECP2 gene mutations.
- Next-generation sequencing (NGS) diagnostics for early identification of rare neurological genetic disorders, enabling timely intervention.
- Engagement in educational initiatives for the broader community about rare neurological genetic disorders, aiming to raise awareness and support affected families.
Neurogene executive team
- Dr. Rachel L. McMinn Ph.D.Founder, Executive Chair & CEO
- Ms. Christine Mikail Cvijic J.D.President & CFO
- Dr. Julie Jordan M.D.Chief Medical Officer
- Dr. Stuart Cobb Ph.D.Chief Scientific Officer
- Ms. Donna M. Cochener-Metcalfe J.D., L.L.M.Senior VP & General Counsel
- Dr. Andrew E. Mulberg CPI, FAAP, M.D.Senior Vice President of Regulatory Affairs, Quality Assurance & Quality Control
- Mr. Ricardo JimenezSenior Vice President of Technical Operations
- Mr. Arvind SreedharanSenior Vice President of Business Operations