Neurogene logo
NGNENeurogene
Trade NGNE now
Neurogene primary media

About Neurogene

Neurogene (NASDAQ:NGNE) is a biotechnology company developing gene therapy treatments for nervous system disorders. They utilize adeno-associated virus (AAV) vectors to deliver corrective genetic material to target cells, potentially offering a new approach to treating neurological conditions. Neurogene's pipeline might focus on treatments for rare or debilitating diseases with limited therapeutic options. While they are still in the pre-commercial stages, with clinical trials ongoing, Neurogene's gene therapy research holds promise for offering life-changing treatments for patients with neurological conditions.

What is NGNE known for?

Snapshot

Public US
Ownership
2018
Year founded
94
Employees
New York, United States
Head office
1 of 3
US Rank
Unknown
Sector
N/A
Sector rank
Loading Map...

Operations

All Locations
New York City, US

Products and/or services of Neurogene

  • Adeno-associated virus (AAV) based gene therapy for neurological diseases, aiming to address genetic disorders by delivering normal genes to patients' cells.
  • Development of a gene therapy for Aspartylglucosaminuria (AGU), a rare lysosomal storage disease, focusing on reducing the accumulation of glycoasparagines.
  • Gene therapy targeting Charcot-Marie-Tooth Disease, specifically focusing on mutations in the GJB1 gene, aiming to restore normal nerve function.
  • Exploration of therapies for Rett Syndrome, a neurodevelopmental disorder, focusing on correcting MECP2 gene mutations.
  • Next-generation sequencing (NGS) diagnostics for early identification of rare neurological genetic disorders, enabling timely intervention.
  • Engagement in educational initiatives for the broader community about rare neurological genetic disorders, aiming to raise awareness and support affected families.

Neurogene executive team

  • Dr. Rachel L. McMinn Ph.D.Founder, Executive Chair & CEO
  • Ms. Christine Mikail Cvijic J.D.President & CFO
  • Dr. Julie Jordan M.D.Chief Medical Officer
  • Dr. Stuart Cobb Ph.D.Chief Scientific Officer
  • Ms. Donna M. Cochener-Metcalfe J.D., L.L.M.Senior VP & General Counsel
  • Dr. Andrew E. Mulberg CPI, FAAP, M.D.Senior Vice President of Regulatory Affairs, Quality Assurance & Quality Control
  • Mr. Ricardo JimenezSenior Vice President of Technical Operations
  • Mr. Arvind SreedharanSenior Vice President of Business Operations

Connect with us

Disclaimer

Grafa is not a financial advisor. You should seek independent, legal, financial, taxation or other advice that relate to your unique circumstances.

Grafa is not liable for any loss caused, whether due to negligence or otherwise arising from the use of or reliance on the information provided directly or indirectly, by use of this platform.