
BioMarin Pharmaceutical (NASDAQ:BMRN) is a biotechnology company dedicated to the development and commercialization of innovative therapies for serious and life-threatening rare genetic diseases. Their operations range from advanced pre-clinical work to the commercial sale of pharmaceuticals. Their projects and objectives focus on providing new treatments for rare metabolic diseases, with a pipeline that includes advanced therapies for phenylketonuria, achondroplasia, and hemophilia, among others. Their mission is to improve the health outcomes and quality of life for these patients, who often have few, if any, medical options, often transforming their lives.